Gene therapy in Glycogen Storage Disorders
Release Date:
Dr Dwight Koeberl joins the podcast to provide some background to gene therapies in Glycogen Storage Disorders, hi-light some ongoing studies and explain why we owe at least some of our knowledge to a menagerie of animal models.
Gene therapy for glycogen storage diseases
Dwight D. Koeberl, et al
https://doi.org/10.1002/jimd.12654
Gene therapy in Glycogen Storage Disorders